Open Actively Recruiting

Multicenter Cure SMA Clinical Data Registry

About

Brief Summary

This study has not yet been registered on ClinicalTrials.gov, which is currently a pre-requisite for display of detailed eligibility criteria.

Eligibility

Minimum Age
N/A
Maximum Age
N/A
Study Stats
Protocol No.
22-5140
Category
Genetic and Rare Diseases
Musculoskeletal Disorders
Principal Investigator
Perry B. Shieh, MD, PhD
Perry B. Shieh, MD, PhD
Neurology, Neuromuscular Medicine
Perry B. Shieh, MD, PhD
Contact
  • Denisse Velazquez
Location
  • UCLA Westwood